Long-Term Clinical Impact of Pseudodeficiency Alleles in Idua

Lauren O apos Grady, Nina B. Gold(Harvard University), Alanna Strong(Children's Hospital of Philadelphia), Inderneel Sahai(Massachusetts General Hospital), Hana Zouk(Harvard University), Jessica A. Gold(Washington University in St. Louis), Emily Zoltick(Harvard Pilgrim Health Care), Wei He(Massachusetts General Hospital), Robert C. Green(Boston University), L. Clarke(University of British Columbia), Emma Perez(Brigham and Women's Hospital), Amel Karaa(Istituto delle Scienze Neurologiche di Bologna)
SSRN Electronic Journal
January 1, 2024
Cited by 0


Related Papers