Enhancing pediatric access to cell and gene therapies

Crystal L. Mackall(Stanford Medicine), Catherine M. Bollard(Children's National), Nancy L. Goodman(Safe Kids Worldwide), Casey Carr(Stanford University), Rebecca Gardner(St. Jude Children's Research Hospital), Rayne H. Rouce(Houston Methodist), Elena Sotillo(Stanford University), Rich Stoner, Fyodor D. Urnov(Innovative Genomics Institute), Alan S. Wayne(University of Southern California), Julie Park(St. Jude Children's Research Hospital), Donald B. Kohn(University of California, Los Angeles)
Nature Medicine
June 17, 2024
Cited by 33

Abstract


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