OP0073 UNRAVELING PATHOPHYSIOLOGY AND HEMATOPOIESIS OF VEXAS SYNDROME BY MULTI-OMICS ANALYSIS AND TARGETED GENE EDITING
C. Campochiaro(Vita-Salute San Raffaele University), G Cavalli(Novartis (Switzerland)), Raffaella Di Micco(Vita-Salute San Raffaele University), Simone Cenci(Vita-Salute San Raffaele University), Ivan Merelli(The San Raffaele Telethon Institute for Gene Therapy), Lorenzo Dagna(Vita-Salute San Raffaele University), Luca Basso‐Ricci(The San Raffaele Telethon Institute for Gene Therapy), Raffaella Molteni(Vita-Salute San Raffaele University), F. Ciceri(Vita-Salute San Raffaele University), Angelica Varesi(The San Raffaele Telethon Institute for Gene Therapy), Eleonora Cantoni(Vita-Salute San Raffaele University), Luciana Albano(University of Campania "Luigi Vanvitelli"), E. Diral(Vita-Salute San Raffaele University), M. Matucci-Cerinic(Vita-Salute San Raffaele University), Daniele Canarutto(Vita-Salute San Raffaele University), Alessandro Aiuti(University of Rome Tor Vergata), Serena Scala(The San Raffaele Telethon Institute for Gene Therapy), Roberta Alfieri(Institute of Biomedical Technologies), Davide Stefanoni(University of Colorado Anschutz Medical Campus), Luigi Naldini(Vita-Salute San Raffaele University), Paola Quaranta(University of Pisa), Guido Pacini(The San Raffaele Telethon Institute for Gene Therapy), A. Tomelleri(Vita-Salute San Raffaele University), Sérgio Ferrari(Azienda USL di Bologna), Astrid Weber(The San Raffaele Telethon Institute for Gene Therapy), Martina Fiumara(The San Raffaele Telethon Institute for Gene Therapy), Armini Alessandro(University of Colorado Anschutz Medical Campus), Mauro Panigada(Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico)
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