OP0073 UNRAVELING PATHOPHYSIOLOGY AND HEMATOPOIESIS OF VEXAS SYNDROME BY MULTI-OMICS ANALYSIS AND TARGETED GENE EDITING
C. Campochiaro(Vita-Salute San Raffaele University), G Cavalli(Novartis (Switzerland)), Raffaella Di Micco(Vita-Salute San Raffaele University), Simone Cenci(Vita-Salute San Raffaele University), Ivan Merelli(The San Raffaele Telethon Institute for Gene Therapy), Lorenzo Dagna(Vita-Salute San Raffaele University), Luca Basso‐Ricci(The San Raffaele Telethon Institute for Gene Therapy), Raffaella Molteni(University of Milan), F. Ciceri(Vita-Salute San Raffaele University), Angelica Varesi(The San Raffaele Telethon Institute for Gene Therapy), Eleonora Cantoni(Vita-Salute San Raffaele University), Luciana Albano(The San Raffaele Telethon Institute for Gene Therapy), E. Diral(Vita-Salute San Raffaele University), M. Matucci-Cerinic(Vita-Salute San Raffaele University), Daniele Canarutto(Vita-Salute San Raffaele University), Alessandro Aiuti(San Raffaele University of Rome), Serena Scala(The San Raffaele Telethon Institute for Gene Therapy), Roberta Alfieri(Institute of Biomedical Technologies), Davide Stefanoni(University of Colorado Anschutz Medical Campus), Luigi Naldini(University of Turin), Paola Quaranta(University of Pisa), Guido Pacini(The San Raffaele Telethon Institute for Gene Therapy), A. Tomelleri(Vita-Salute San Raffaele University), Sérgio Ferrari(University of Modena and Reggio Emilia), Astrid Weber(The San Raffaele Telethon Institute for Gene Therapy), Martina Fiumara(Vita-Salute San Raffaele University), Armini Alessandro(University of Colorado Anschutz Medical Campus), Mauro Panigada(Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico)
Cited by 0
Related Papers
Efficient transfer, integration, and sustained long-term expression of the transgene in adult rat brains injected with a lentiviral vector.
|Proceedings of the National Academy of Sciences|1996|1.5k
Lentiviral Hematopoietic Stem Cell Gene Therapy in Patients with Wiskott-Aldrich Syndrome
|Science|2013|1k
Gene Therapy for Immunodeficiency Due to Adenosine Deaminase Deficiency
|New England Journal of Medicine|2009|1k
Scatter factor and hepatocyte growth factor are indistinguishable ligands for the MET receptor.
|The EMBO Journal|1991|667