WS05.04 SPL84 efficient and durable effect, restoring 3849 +10 kb C-to-T mutated CFTR, when treated through the apical side of primary HBE cells
E. Ozeri Galai(Azrieli College of Engineering Jerusalem), Batsheva Kerem(Hebrew University of Jerusalem), Martin Mense(Cystic Fibrosis Foundation), Justin Chin(Cystic Fibrosis Foundation), Yanbo Cheng(South China Agricultural University), K. Coote(Cystic Fibrosis Foundation), Yifat S. Oren(Hebrew University of Jerusalem), C.D. Stampfer(Azrieli College of Engineering Jerusalem)
Cited by 0
Related Papers
Dual SMAD Signaling Inhibition Enables Long-Term Expansion of Diverse Epithelial Basal Cells
|Cell stem cell|2016|409
Selective Elimination of Human Pluripotent Stem Cells by an Oleate Synthesis Inhibitor Discovered in a High-Throughput Screen
|Cell stem cell|2013|307
CFTR modulator theratyping: Current status, gaps and future directions
|Journal of Cystic Fibrosis|2018|288
GmWRKY16 Enhances Drought and Salt Tolerance Through an ABA-Mediated Pathway in Arabidopsis thaliana
|Frontiers in Plant Science|2019|226