Bone-marrow-homing lipid nanoparticles for genome editing in diseased and malignant haematopoietic stem cells
Xizhen Lian(The University of Texas Southwestern Medical Center), Sumanta Chatterjee(The University of Texas Southwestern Medical Center), Yehui Sun(The University of Texas Southwestern Medical Center), Sean A. Dilliard(The University of Texas Southwestern Medical Center), Stephen D. Moore(The University of Texas Southwestern Medical Center), Yufen Xiao(The University of Texas Southwestern Medical Center), Xiaoyan Bian(The University of Texas Southwestern Medical Center), Kohki Yamada(The University of Texas Southwestern Medical Center), Yun‐Chieh Sung(The University of Texas Southwestern Medical Center), Rachel M. Levine(St. Jude Children's Research Hospital), Kalin Mayberry(St. Jude Children's Research Hospital), Samuel John(The University of Texas Southwestern Medical Center), Xiaoye Liu(The University of Texas Southwestern Medical Center), Caroline Smith(The University of Texas Southwestern Medical Center), Lindsay T. Johnson(The University of Texas Southwestern Medical Center), Xu Wang(The University of Texas Southwestern Medical Center), Cheng Cheng Zhang(The University of Texas Southwestern Medical Center), David R. Liu(Broad Institute), Gregory A. Newby(Johns Hopkins University), Mitchell J. Weiss(St. Jude Children's Research Hospital), Jonathan Yen(St. Jude Children's Research Hospital), Daniel J. Siegwart(Southwestern Medical Center)
Cited by 107Open Access