Modified lentiviral globin gene therapy for pediatric β0/β0 transfusion-dependent β-thalassemia: A single-center, single-arm pilot trial

Shiqi Li(nLIGHT (United States)), Yujia Cai(Shanghai Jiao Tong University), Wei Tang(Zhejiang University of Technology), Sikai Ling(Shanghai Jiao Tong University), Yingnian Chen, Zhongtao Yuan, Ying Dai, Sanbin Wang, Xiaoyuan Wang(Regend Therapeutics (China)), Lihua Zhang(Regend Therapeutics (China)), Dawei Wang(RWTH Aachen University), Lin Liu, Le Luo, Fangyuan Hao(Regend Therapeutics (China)), Sujiang Zhang(Shanghai Institute of Hematology), Lin Zhang(The University of Melbourne), Yu Li, Liufan Yin, Dongjie Deng, Lvzhe Chen
Cell stem cell
May 16, 2024
Cited by 77


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