Biallelic mutations in SUPV3L1 cause an inherited neurodevelopmental disorder with variable leukodystrophy due to aberrant mitochondrial double stranded RNA processing

Lydia Green, Yanick J. Crow(Institute of Genetics and Cancer), David H. Dockrell(NHS Lothian), Annarita Scardamaglia(Queen Mary University of London), Maha S. Zaki(National Water Research Center), Mark A. Tarnopolsky(McMaster University), Katrin Õunap(Tartu University Hospital), Almundher Al‐Maawali(Sultan Qaboos University Hospital), Mina Zamani(Shahid Chamran University of Ahvaz), Stéphanie Efthymiou(Queen Mary University of London), Khalid Al‐Thihli(Sultan Qaboos University Hospital), Stephan Züchner(University of Miami), Andrew G. L. Douglas(Oxford University Hospitals NHS Trust), Colin A. Johnson(University of Leeds), Kristian Tveten(Telemark Hospital), Daniel G. Calame, Kristen Fisher(Baylor College of Medicine), Prab Prabhakar(Great Ormond Street Hospital), Saeid Sadeghian(Ahvaz Jundishapur University of Medical Sciences), Tahere Seifi(Shahid Chamran University of Ahvaz), Eamonn Sheridan(St James's University Hospital), Erum Afzal(National Institute of Child Health), Stephen A. Renshaw(University of Sheffield), Marilena Elpidorou, Elizabeth C. Low, Clément Prouteau(Northwestern University), Ailsa M.S. Rose, Sarah A. Harris, Lauren Brady(McMaster Children's Hospital), Marine Tessarech(Centre National de la Recherche Scientifique), Céline Bris(Université d'Angers), Noémie Hamilton, Hamid Galehdari(Shahid Chamran University of Ahvaz), Gillian Rice(Manchester Academic Health Science Centre), Daniel Warren, Geoffrey Wells, Carla Roca-Bayerri, Reza Azizi Malamiri(Ahvaz Jundishapur University of Medical Sciences), Henry Houlden(Queen Mary University of London), Emma Wakeling(Northwick Park Hospital), Reza Maroofian(University College London), Inger Sandvig, Gholamreza Shariati(Ahvaz Jundishapur University of Medical Sciences), Stone Elworthy, Amna Al‐Futaisi(Sultan Qaboos University Hospital), John H. Livingston(Montreal Neurological Institute and Hospital), Mario Sa, Erica Harris(University of Leeds), Sana Al‐Zuhaibi(Sultan Qaboos University Hospital), Iván K. Chinn(Baylor College of Medicine)
Research Square
May 10, 2024
Cited by 0


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