Gene Editing for <i>CEP290</i> -Associated Retinal Degeneration

Eric A. Pierce(Broad Institute), Mark E. Pennesi(University of Pennsylvania), Alia Rashid(Penn Presbyterian Medical Center), Keunpyo Kim(Penn Presbyterian Medical Center), Bright S. Ashimatey(Johns Hopkins University), Michael Jaskolka(Editas Medicine (United States)), Steven T. Bailey(Oregon Health & Science University), Andreas Lauer(Legacy Health), Albert M. Maguire(Children's Hospital of Philadelphia), R Myers(Penn Presbyterian Medical Center), Tomás S. Alemán(Children's Hospital of Philadelphia), Byron L Lam(Penn Presbyterian Medical Center), Jason Comander(Massachusetts Eye and Ear Infirmary)
New England Journal of Medicine
May 6, 2024
Cited by 209


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