Genome engineering with Cas9 and AAV repair templates generates frequent concatemeric insertions of viral vectors

Fabian P. Suchy(Stanford University), Hiromitsu Nakauchi(Japan Science and Technology Agency), Maimi Higuchi(Stanford University), Carsten T. Charlesworth(Stanford University), Jinyu Zhang(State Administration of Traditional Chinese Medicine of the People's Republic of China), Mark A. Kay(Pediatrics and Genetics), Ian Hsu(University of Oxford), Daiki Karigane(Keio University), Amy C. Fan(Stanford University), Katja Pekrun(Pediatrics and Genetics), Adam C. Wilkinson(Wellcome/MRC Cambridge Stem Cell Institute), Ravindra Majeti(California Institute for Regenerative Medicine), Toshinobu Nishimura(Stanford University), T. Nishimura(Hokkaido University), Yusuke Nakauchi(Stanford University), Joydeep Bhadury(Stanford University)
Nature Biotechnology
April 8, 2024
Cited by 56


Related Papers