A novel deep intronic variant introduce dystrophin pseudoexon in Becker muscular dystrophy: A case report

Chang Liu(Weifang Medical University), Yanyu Lu(Peking University), Fangfang Niu(Peking University), Xin-Chao Cheng(Southwest University), Lingchao Meng(Peking University), Jianwen Deng(Peking University), Yun Yuan(Peking University), Chengyue Sun, Yawen Zhao(Peking University), Haiyan Yu(Chinese Academy of Sciences), Zhihao Xie(Second Affiliated Hospital of Jilin University), Zhiying Xie(Peking University), Zhaoxia Wang(Hefei University)
Heliyon
March 1, 2024
Cited by 3


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