Advancing rare disease treatment: EMA’s decade-long insights into engineered adoptive cell therapy for rare cancers and orphan designation
Maria Elisabeth Kalland(European Medicines Agency), Segundo Mariz(European Medicines Agency), Dinah Duarte(National Laboratory for Civil Engineering), Armando Magrelli(European Medicines Agency), Darius Matusevičius(European Medicines Agency), Gloria M. Palomo(Agencia Española de Medicamentos y Productos Sanitarios), Dinko Vitezić(University of Rijeka), Tomás Pose‐Boirazian(European Medicines Agency), Kristina Larsson(European Medicines Agency), Frauke Naumann‐Winter(Federal Institute for Drugs and Medical Devices), Enrico Costa(Brigham and Women's Hospital), Eva Malikova(European Medicines Agency), Violeta Stoyanova‐Beninska(European Medicines Agency)
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