High-dose systemic adeno-associated virus vector administration causes liver and sinusoidal endothelial cell injury

Juliette Hordeaux(University of Pennsylvania), Jason Lamontagne(University of Pennsylvania), Chunjuan Song(University of Pennsylvania), George Buchlis(University of Pennsylvania), Cecilia Dyer(University of Pennsylvania), Elizabeth L. Buza(University of Pennsylvania), Ali Ramezani(University of Pennsylvania), Erik Wielechowski(University of Pennsylvania), Jenny A. Greig(University of Pennsylvania), Jessica A. Chichester(University of Pennsylvania), Peter Bell(University of Pennsylvania), James M. Wilson(University of Pennsylvania)
Molecular Therapy
February 6, 2024
Cited by 66Open Access
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