Development of a rigorous approach for retrospective natural history studies in leukodystrophies
Anjana Sevagamoorthy(Children's Hospital of Philadelphia), Laura Adang(Children's Hospital of Philadelphia), Sarah Woidill(Children's Hospital of Philadelphia), Francesco Gavazzi(Children's Hospital of Philadelphia), Omar Sherbini(Children's Hospital of Philadelphia), Nicholson Modesti(Children's Hospital of Philadelphia), Ariel Vincent(Children's Hospital of Philadelphia), Amy Pizzino(Children's Hospital of Philadelphia), Russel D'Aiello(Children's Hospital of Philadelphia), Sylvia Mutua(Children's Hospital of Philadelphia), Johanna Schmidt(Counseling Center), Justine Shults(Children's Hospital of Philadelphia), Emily Yu(Children's Hospital of Philadelphia), Adeline Vanderver(Children's Hospital of Philadelphia)
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