Validation of GMFC-MLD scale as a measure of gross motor function in metachromatic leukodystrophy
Sylvia Mutua(Children's Hospital of Philadelphia), Laura Adang(Children's Hospital of Philadelphia), Nivedita Thakur(Montreal Children's Hospital), Adeline Vanderver(Children's Hospital of Philadelphia), Anjana Sevagamoorthy(Children's Hospital of Philadelphia), Sarah Woidill(Children's Hospital of Philadelphia), Samuel Groeschel(University of Tübingen), Francesco Gavazzi(Children's Hospital of Philadelphia), Francesca Fumagalli(Vita-Salute San Raffaele University), Lisa Emrick(Baylor College of Medicine), Christiane Kehrer(University Children's Hospital Tübingen), Emily Yu(Children's Hospital of Philadelphia), Justine Shults(Children's Hospital of Philadelphia), Chloe Stutterd(Royal Children's Hospital), Geneviève Bernard(McGill University)
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