Audiology assessment of participants in CAMPSIITE™, a phase I/II/III study of RGX-121 in neuronopathic MPS II

Nidal Boulos, Paulo Falabella, Patricia Roush(University of North Carolina at Chapel Hill), Dawn Phillips(ProterixBio (United States)), Ariana Pjetri, Laura Rosa Pisani(Regenxbio (United States))
Molecular Genetics and Metabolism
January 31, 2024
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