Advancing in vivo modelling and delivery systems for triplet repeat expansion‐mediated corneal endothelial dystrophy: Implications in Anti‐miR therapy
Diego Piqueras‐Losilla(SOM Biotech (Spain)), Estefanía Cerro‐Herros(SOM Biotech (Spain)), Isabel Campillo(SOM Biotech (Spain)), Beatriz Llamusí(SOM Biotech (Spain)), Geneviève Gourdon(Inserm), Milagros Rocha‐Barajas(Fundación para el Fomento de la Investigación Sanitaria y Biomédica de la Comunitat Valenciana), Laura Perea‐Galera(Fundación para el Fomento de la Investigación Sanitaria y Biomédica de la Comunitat Valenciana), Clara Barbera‐Fuset(Fundación José Ortega y Gasset-Gregorio Marañón), María José Roig-Revert(Fundación para el Fomento de la Investigación Sanitaria y Biomédica de la Comunitat Valenciana), Cristina Peris‐Martínez(Universitat de València), Aline Huguet(Inserm), Sandra López‐Domènech(Fundación para el Fomento de la Investigación Sanitaria y Biomédica de la Comunitat Valenciana)
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