Identification of GM1-Ganglioside Secondary Accumulation in Fibroblasts from Neuropathic Gaucher Patients and Effect of a Trivalent Trihydroxypiperidine Iminosugar Compound on Its Storage Reduction
Costanza Ceni(University of Florence), Martino Calamai(National Research Council), Rodolfo Tonin(Meyer Children's Hospital), Francesca Clemente(University of Florence), Camilla Matassini(University of Florence), Francesca Mangiavacchi(University of Florence), Anna Caciotti(Meyer Children's Hospital), Federica Feo(Meyer Children's Hospital), Amelia Morrone(Meyer Children's Hospital), Francesca Cardona(University of Florence), Domenico Coviello(Istituto Giannina Gaslini)
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