Event-free survival of maralixibat-treated patients with Alagille syndrome compared to a real-world cohort from GALA
Bettina E. Hansen(Aarhus University), Shannon M. Vandriel(University of Toronto), Emmanuel Gonzalès(Université Paris-Sud), Saul J. Karpen(Karolinska University Hospital), Pamela Vig(Pinnacle Clinical Research), Tanguy Demaret(UCLouvain), Catalina Jaramillo(Primary Children's Hospital), Björn Fischler(Karolinska University Hospital), Henrik Arnell(Karolinska University Hospital), Jeffrey A. Feinstein(Lucile Packard Children's Hospital), Will Garner, Pamela L. Valentino(Yale University), Henkjan J. Verkade(University Medical Center Groningen), Amin J. Roberts(Starship Children's Health), Rubén E. Quirós‐Tejeira(Children's Hospital & Medical Center), Winita Hardikar(Royal Children's Hospital), Étienne Sokal(Cliniques Universitaires Saint-Luc), Emanuele Nicastro(Ospedale Papa Giovanni XXIII), Sahana Shankar(Narayana Health), Dorota Gliwicz‐Miedzińska(Children's Memorial Health Institute), Noelle H. Ebel(Stanford University), Ryan T. Fischer(Children's Mercy Hospital), Kathleen B. Schwarz(Rady Children's Hospital-San Diego), Jérôme Bouligand(Assistance Publique – Hôpitaux de Paris), Lorenzo D’Antiga(Ospedale Papa Giovanni XXIII), Helen Evans(Statistics New Zealand), Pier Luigi Calvo(University of Turin), Dominique Debray(Hôpital Necker-Enfants Malades), Shikha S. Sundaram(Children's Hospital Colorado), James E. Squires(Children's Hospital of Pittsburgh), Kathleen M. Loomes(Children's Hospital of Philadelphia), Piotr Czubkowski(Children's Memorial Health Institute), Antal Dezsőfi(Semmelweis University), Douglas Mogul(Johns Hopkins Medicine), Alexander Chaidez(Children's Hospital Colorado), Catherine Larson‐Nath(University of Minnesota), René Romero(Emory University), Maria Rogalidou(Unknown), Irena Jankowska(Children's Memorial Health Institute), Emmanuel Jacquemin(Inserm), Michael Stormon(Children's Hospital at Westmead), Florence Lacaille(Hôpital Necker-Enfants Malades), Elizabeth B. Rand, Henry C. Lin(Oregon Health & Science University), Palaniswamy Karthikeyan(Leeds Teaching Hospitals NHS Trust), David A. Piccoli(Children's Hospital of Philadelphia), Susan Siew(Children's Hospital at Westmead), Giuseppe Indolfi(Meyer Children's Hospital), M. Kyle Jensen(University of Utah)
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