EPH85 Clinical Burden of GM2 Gangliosidoses in the United States (US): A Retrospective Observational Cohort Study Using Electronic Health Records (EHR)
M.B. Rodríguez(Sanofi (United States)), Cynthia J. Tifft(Children's National), Marie Fournier(Sanofi (France)), Rui Zheng(Zhejiang University), Natalia Petruski‐Ivleva(AVEO Oncology (United States)), Julie Kissell, Isabela Batsu(Sanofi (United States)), Siddhi Umarje, Duane Madziva(Sanofi (United States)), A.L. Flores(Sanofi (United States)), Ruth Pulikottil-Jacob(University of Warwick)
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