Characterization of central manifestations in patients with Niemann-Pick disease type C
Raquel van Gool(Boston Children's Hospital), Jaymin Upadhyay(Boston Children's Hospital), Mariesa Cay(Boston Children's Hospital), Jason A. Tourville(Boston University), Emma Golden(Boston Children's Hospital), Boyu Ren(Harvard University), Leo Zekelman(Brigham and Women's Hospital), Adam P. Vogel(Synlab Czech (Czechia)), Benjamin D. Goodlett(Boston Children's Hospital), Walla Al‐Hertani(Dalhousie University), Lauren J. O’Donnell(Brigham and Women's Hospital), Olaf A. Bodamer(Broad Institute), Sneham Tiwari(Boston Children's Hospital), Fan Zhang(University of Bristol), Edward Yang(Insper)
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