AAV-based gene therapy ameliorated CNS-specific GPI defect in mouse models
Yoshiko Murakami(The University of Osaka), Taroh Kinoshita(Suita Municipal Hospital)
Cited by 9
Related Papers
A GPI processing phospholipase A2, PGAP6, modulates Nodal signaling in embryos by shedding CRIPTO
|The Journal of Cell Biology|2016|49
Accumulated precursors of specific GPI-anchored proteins upregulate GPI biosynthesis with ARV1
|The Journal of Cell Biology|2023|29
Establishment of mouse model of inherited PIGO deficiency and therapeutic potential of AAV-based gene therapy
|Nature Communications|2022|22
PGAP6, a GPI-specific phospholipase A2, has narrow substrate specificity against GPI-anchored proteins
|Journal of Biological Chemistry|2020|19
Loss of the N-acetylgalactosamine side chain of the GPI-anchor impairs bone formation and brain functions and accelerates the prion disease pathology
|Journal of Biological Chemistry|2022|15