Single intravitreal administration of a tetravalent siRNA exhibits robust and efficient gene silencing in mouse and pig photoreceptors

Shun-Yun Cheng(University of Massachusetts Chan Medical School), Claudio Punzo(University of Massachusetts Chan Medical School)

Molecular Therapy — Nucleic Acids

December 5, 2023

10.1016/j.omtn.2023.102088

Cited by 16

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