Unraveling Pathophysiology and Hematopoiesis of Vexas Syndrome By Multi-Omics Analyses and Targeted Gene Editing
Raffaella Molteni(Vita-Salute San Raffaele University), Samuele Ferrari(Vita-Salute San Raffaele University), Pamela Quaranta(The San Raffaele Telethon Institute for Gene Therapy), Raffaella Di Micco(Vita-Salute San Raffaele University), Simone Cenci(Vita-Salute San Raffaele University), Elisa Diral(Vita-Salute San Raffaele University), Fabio Ciceri(Vita-Salute San Raffaele University), Ivan Merelli(The San Raffaele Telethon Institute for Gene Therapy), Lorenzo Dagna(Vita-Salute San Raffaele University), Giulio Cavalli(Istituto di Ricovero e Cura a Carattere Scientifico San Raffaele), Luca Basso‐Ricci(The San Raffaele Telethon Institute for Gene Therapy), Alessandro Tomelleri(Vita-Salute San Raffaele University), Corrado Campochiaro(Vita-Salute San Raffaele University), Luisa Albano(The San Raffaele Telethon Institute for Gene Therapy), Marco Matucci‐Cerinic(Vita-Salute San Raffaele University), Angelica Varesi(The San Raffaele Telethon Institute for Gene Therapy), Maddalena Panigada(Vita-Salute San Raffaele University), Angelo D’Alessandro(University of Colorado Anschutz Medical Campus), Eleonora Cantoni(Vita-Salute San Raffaele University), Daniele Canarutto(Vita-Salute San Raffaele University), Alessandro Aiuti(University of Rome Tor Vergata), Serena Scala(The San Raffaele Telethon Institute for Gene Therapy), Roberta Alfieri(Institute of Biomedical Technologies), Davide Stefanoni(University of Colorado Anschutz Medical Campus), Alessandra Weber(Vita-Salute San Raffaele University), Luigi Naldini(Vita-Salute San Raffaele University), Martina Fiumara(The San Raffaele Telethon Institute for Gene Therapy)
Cited by 2
Related Papers
Retinoic Acid and Arsenic Trioxide for Acute Promyelocytic Leukemia
|New England Journal of Medicine|2013|1.6k
Efficient transfer, integration, and sustained long-term expression of the transgene in adult rat brains injected with a lentiviral vector.
|Proceedings of the National Academy of Sciences|1996|1.5k
Lentiviral Hematopoietic Stem Cell Gene Therapy in Patients with Wiskott-Aldrich Syndrome
|Science|2013|1k
Gene Therapy for Immunodeficiency Due to Adenosine Deaminase Deficiency
|New England Journal of Medicine|2009|1k