Spliceosome malfunction causes neurodevelopmental disorders with overlapping features

Dong Li(Children's Hospital of Philadelphia), Jessica Douglas(Boston University), Mark R. Battig(Children's Hospital of Philadelphia), Emanuele Agolini(Bambino Gesù Children's Hospital), Gijs van Haaften, Andrea Petersen(Legacy Emanuel Medical Center), Antonio Novelli(Bambino Gesù Children's Hospital), Michael J. Lyons, Mark A. Tarnopolsky(McMaster University), Khanh Lai(University of Utah), Daniëlle G.M. Bosch(Erasmus MC), Rachel Palmquist(University of Utah), Michael March(Children's Hospital of Philadelphia), Radka Kremlíková Pourová(Charles University), Martin Schwarz(Boston Children's Hospital), Qin Wang(Children's Hospital of Philadelphia), Tuğçe B. Balcı(Western University), Cuiping Hou(Children's Hospital of Philadelphia), Beth Keena(Children's Hospital of Philadelphia), Marcello Scala(Muscular Dystrophy Association), Maria Lisa Dentici(Casa Sollievo della Sofferenza), Hanna Faghfoury(University Health Network), Margaret Harr(Children's Hospital of Philadelphia), Lea Kristin Parsley(Mercy Health System), Michele Iacomino(Istituto Giannina Gaslini), Gabrielle Lemire(Broad Institute), Timothy J. Maarup(Kaiser Permanente), Raymond J. Louie(Greenwood Genetic Center), Anushree Aneja(Children's Hospital of Philadelphia), Leslie Granger(Legacy Emanuel Medical Center), Melissa Byler(SUNY Upstate Medical University), Federico Zara(Istituto Giannina Gaslini), Robert Roger Lebel(SUNY Upstate Medical University), Lauren Brady(McMaster Children's Hospital), Kym M. Boycott(University of Ottawa), Allan Bayat(University of Copenhagen), Nora O’Connor(Children's Hospital of Philadelphia), Gemma Aznar‐Laín, Michael Parker(Wellcome Sanger Institute), Miroslava Hančárová(Charles University), Meghan C. Towne(Ambry Genetics (United States)), Šárka Bendová(Charles University), Yijing Zhou(Children's Hospital of Philadelphia), Pasquale Striano(Istituto Giannina Gaslini), Luis A. Pérez‐Jurado(Universitat Pompeu Fabra), Elizabeth Bhoj(Children's Hospital of Philadelphia), Meredith S. Wright(Children’s Institute), Megan Li(Invitae (United States)), Annina H. Cooper(Kaiser Permanente), Zdeněk Sedláček(Charles University)
Journal of Clinical Investigation
November 14, 2023
Cited by 44


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