AAV-SPL 2.0, a Modified Adeno-Associated Virus Gene Therapy Agent for the Treatment of Sphingosine Phosphate Lyase Insufficiency Syndrome

Ranjha Khan(University of California, San Francisco), Julie D. Saba(UCSF Benioff Children's Hospital)
International Journal of Molecular Sciences
October 25, 2023
Cited by 8


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