Establishing Patient-Centered Outcomes for MCT8 Deficiency: Stakeholder Engagement and Systematic Literature Review
Nina‐Maria Wilpert(Humboldt-Universität zu Berlin), Markus Schuelke(Humboldt-Universität zu Berlin), Davide Tonduti, Ylenia Vaia, Catherine Sarret(Institut Pascal), Heiko Krude(Humboldt-Universität zu Berlin)
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