Integrome signatures of lentiviral gene therapy for SCID-X1 patients

Koon‐Kiu Yan(St. Jude Children's Research Hospital), Jiyang Yu(Columbia University Irving Medical Center), Jennifer M. Puck(University of California, San Francisco), Timothy Lockey(St. Jude Children's Research Hospital), Michael M. Meagher(St. Jude Children's Research Hospital), Aimee C. Talleur(St. Jude Children's Research Hospital), John Easton(St. Jude Children's Research Hospital), Jose Condori(St. Jude Children's Research Hospital), Ewelina Mamcarz(National Institutes of Health), Deanna Langfitt(St. Jude Children's Research Hospital), Bridget Shaner(St. Jude Children's Research Hospital), Lance E. Palmer(St. Jude Children's Research Hospital), Robert E. Throm(St. Jude Children's Research Hospital), Liang Ding(Qingdao University), Morton J. Cowan(Blood Systems Research Institute), Stephen Gottschalk(St. Jude Children's Research Hospital), Sheng Zhou(St. Jude Children's Research Hospital), Yogesh Dhungana(St. Jude Children's Research Hospital), Jean‐Yves Métais(National Institutes of Health), Hao Shi(St. Jude Children's Research Hospital), Sheetal Bhatara(St. Jude Children's Research Hospital), Zhijun Ma(St. Jude Children's Research Hospital), Francesca Ferrara(St. Jude Children's Research Hospital), Bensheng Ju(St. Jude Children's Research Hospital), Isabel Risch(St. Jude Children's Research Hospital)
Science Advances
October 6, 2023
Cited by 9


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