Efficacy and safety of the neonatal Fc receptor inhibitor efgartigimod in adults with primary immune thrombocytopenia (ADVANCE IV): a multicentre, randomised, placebo-controlled, phase 3 trial

Catherine M. Broome(Georgetown University), Vickie McDonald(Barts Health NHS Trust), Yoshitaka Miyakawa(Saitama Medical University Hospital), Monica Carpenedo(Azienda Ospedaliera San Gerardo), David J. Kuter(Massachusetts General Hospital), Hanny Al‐Samkari(Massachusetts General Hospital), James B. Bussel(Cornell University), Marie Godar(Argenx (Belgium)), Jaume Ayguasanosa(Argenx (Belgium)), Kristof De Beuf(Argenx (Belgium)), Francesco Rodeghiero(Ospedale San Bortolo), Marc Michel(Université Paris-Est Créteil), Adrian C. Newland(Queen Mary University of London), Michael Fillitz, Paul Knoebl, Stef Meers, Ismail Amine, Jaromír Gumulec, Antonín Hluší, Jiřı́ Mayer, Philippe Quittet, Jean‐François Viallard, M Betaneli, I Datikashvili-David, Genadi Iosava, Levan Makhaldiani, László Rejtő, Nino Sharashenidze, Stefanie Groepper, Alexander Röth, Aryan Hamed, Árpád Illés, Monica Carpenedo(Azienda Ospedaliera San Gerardo), Andrea Artoni, Monica Bocchia(Azienda Ospedaliera San Gerardo), Barbara Gamberi, Alessandra Borchiellini, Esther Natalie Olíva, Andrea Patriarca, Simona Tomassetti, Yoshitaka Miyakawa(Saitama Medical University Hospital), Kiyoshi Ando, Hiroshi Handa, Shinya Katsutani, Kaichi Nishiwaki, Shoko Ito, Tomoki� Ito, Fransien de Boer, A.J. Gerard Jansen, Hanna Ciepłuch, Szymon Fornagiel, Sebastian Grosicki, Maria Soroka‐Wojtaszko, Jacek Treliński, Б. А. Бакиров, Elena Borisenkova, Elena Volodicheva, Yuri Shatokhin, Andrey Proydakov, Maria Aranzazu Alonso, María Eva Mingot‐Castellano, Blanca Sánchez‐González, David Valcarcel Ferreiras(Massachusetts General Hospital), Meltem Aylı, Tuba Hacıbekiroğlu, Ahmet Muzaffer Demir, Meliha Nalçacı, Mehmet Sönmez, Anıl Tombak, Selami Koçak Toprak, Burhan Turgut, Filiz Vural, Münci Yağcı, Fevzi Altuntaş, Mehmet Turgut, Emın Kaya, Nataliya Romanyuk, Vickie McDonald(Barts Health NHS Trust), Syed Rashid Saeed Kazmi, Catherine M. Broome(Georgetown University), Spero R. Cataland, Ketan Doshi, Steven R. Lentz, Michael Boxer, Richard Rosenberg
The Lancet
September 28, 2023
Cited by 88Open Access
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