Treatment of monogenic and digenic dominant genetic hearing loss by CRISPR-Cas9 ribonucleoprotein delivery in vivo

Yong Tao(Shanghai Ninth People's Hospital), Zheng‐Yi Chen(Massachusetts Eye and Ear Infirmary), Xue Gao(Xijing Hospital), Verónica Lamas(Massachusetts Eye and Ear Infirmary), Wenliang Zhu(Kyoto Institute of Technology), John A. Zuris(Howard Hughes Medical Institute), Wan Du(University of Michigan), Weijia Kong(Wuhan Union Hospital), Johnny H. Hu(Howard Hughes Medical Institute), Benjamin P. Kleinstiver(Harvard University), David R. Liu(Broad Institute), Hao Wu(Shanghai Jiao Tong University), Yilai Shu(Fudan University), Charles Pei(Massachusetts Eye and Ear Infirmary), Yiran Li(Morinaga (Japan)), David B. Thompson(Howard Hughes Medical Institute), Madelynn N. Whittaker(Cardiovascular Institute of the South), Xuezhong Liu(University of Miami), Arun Prabhu Rameshbabu(Massachusetts Eye and Ear Infirmary)
Nature Communications
August 15, 2023
Cited by 49


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