OC7 Maralixibat-treated patients with Alagille syndrome demonstrate event-free survival in a natural history comparison with patients with from the GALA database: application of real-world evidence analytics

BE Hansen(University Health Network), Björn Fischler(Karolinska University Hospital), Willa Y. Garner, DB Mogul, Pamela Vig(Pinnacle Clinical Research), Tanguy Demaret(UCLouvain), Henrik Arnell(Karolinska University Hospital), Henkjan J. Verkade(University Medical Center Groningen), Winita Hardikar(Royal Children's Hospital), Étienne Sokal(Cliniques Universitaires Saint-Luc), Emanuele Nicastro(Ospedale Papa Giovanni XXIII), Sahana Shankar(Narayana Health), Alexander Chaidez(Children's Hospital Colorado), Kathleen B. Schwarz(Rady Children's Hospital-San Diego), Jérôme Bouligand(Assistance Publique – Hôpitaux de Paris), Lorenzo D’Antiga(Ospedale Papa Giovanni XXIII), Dominique Debray(Hôpital Necker-Enfants Malades), NH Ebel(Stanford University), Piotr Czubkowski(Children's Memorial Health Institute), Catherine Larson‐Nath(University of Minnesota), René Romero(Emory University), Maria Rogalidou(Unknown), Irena Jankowska(Children's Memorial Health Institute), Emmanuel Jacquemin(Inserm), Michael Stormon(Children's Hospital at Westmead), Carlos Mario Zapata Jaramillo(Universidad Nacional de Colombia), Florence Lacaille(Hôpital Necker-Enfants Malades), D Gliwicz-Miedzi nacute ska(Children's Memorial Health Institute), SM Vandriel(University of Toronto), R. Daryl Fischer(Children's Mercy Hospital), P. Karthikeyan(Saveetha University), S. Meenakshi Sundaram(Children's Hospital Colorado), KM Loomes(Children's Hospital of Philadelphia), AJ Roberts(Starship Children's Health), PL. Calvo(Azienda Ospedaliera Citta' della Salute e della Scienza di Torino), JA Feinstein(Lucile Packard Children's Hospital), S KARPEN(Emory University), H. M. Evans(Swansea University), EB Rand(Children's Hospital of Philadelphia), PL Valentino(Seattle Children's Hospital), JE Squires(University of Pittsburgh), EM Gonzales(Inserm), RE Quiros-Tejeira(Children's Hospital & Medical Center), DA Piccoli(Children's Hospital of Philadelphia), H. J. Lin(Oregon Health & Science University), Susan Siew(Children's Hospital at Westmead), Giuseppe Indolfi(Meyer Children's Hospital), MK Jensen(Primary Children's Hospital)
Abstracts
July 1, 2023
Cited by 0


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