A framework for individualized splice-switching oligonucleotide therapy
Jin‐Kuk Kim(Hanyang University), Timothy W. Yu(Boston Children's Hospital), Sijae Woo(Korea Advanced Institute of Science and Technology), Peter J. Park(Harvard University), Christelle Moufawad El Achkar(Harvard University), Lynn Wein Bush(Boston Children's Hospital), Laura Cornelissen(Harvard University), Ashley Kuniholm(Boston Children's Hospital), Tojo Nakayama(Boston Children's Hospital), Eunjung Alice Lee(Broad Institute), Jennifer Karlin Thornton, Brad Margus, Minh Anh Nguyen(Boston Children's Hospital), Charles B. Berde(Boston Children's Hospital), Carolina Donado(Pain and Rehabilitation Medicine), Renata L. DiDonato(Institut thématique Génétique, génomique et bioinformatique), Aubrie Soucy(Institut thématique Génétique, génomique et bioinformatique), Claudia Lentucci(Boston Children's Hospital), Diana Chin(Boston Children's Hospital), Victoria Suslovitch(Boston Children's Hospital), Boxun Zhao(Broad Institute), Olivia Riccardi(Boston Children's Hospital), Zane S. Dash(Boston Children's Hospital), Kamli N. W. Faour(Boston Children's Hospital), Chunguang April Hu(Boston Children's Hospital), Al Patterson(Harvard University), Anthony Philippakis(Google (United States)), Danielle A. Friedman(Boston Children's Hospital), Claudio M. de Gusmão(Boston Children's Hospital)
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