Unexpected Death of a Duchenne Muscular Dystrophy Patient in an N-of-1 Trial of rAAV9-delivered CRISPR-transactivator
Angela Lek(Muscular Dystrophy Association), Terence R. Flotte(University of Massachusetts Chan Medical School), Keith A. Sutton(Charles River Laboratories (United States)), Allison M. Keeler(University of Massachusetts Chan Medical School), Chrystalle Katte Carreon(Boston Children's Hospital), Monkol Lek(Massachusetts General Hospital), Meghan Blackwood(University of Massachusetts Chan Medical School), Brenda Wong(Cincinnati Children's Hospital Medical Center), Keryn G. Woodman(Yale University), Hart G.W. Lidov(Boston Children's Hospital), Juan Putra(Boston Children's Hospital), Janelle M. Spinazzola(Boston Children's Hospital), Joan M. LaRovere(Boston Children's Hospital), Shestruma Parajuli(University of Massachusetts Chan Medical School), Shushu Huang(Yale University), Katelyn Sylvia(University of Massachusetts Chan Medical School), Kaiyue Ma(International Peace Maternity & Child Health Hospital), Lauren Page Black(Charles River Laboratories (United States)), Danielle Kokoski(University of Massachusetts Chan Medical School), Diane Baulderson, Rebecca Artinian(University of Massachusetts Chan Medical School), Ana Rita Batista(University of Massachusetts Chan Medical School), Sander Pajusalu(MACOM (United States)), Richard Horgan, T. F. Gallagher(University of Massachusetts Chan Medical School)
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