GAA-<i>FGF14</i> ataxia (SCA27B): phenotypic profile, natural history progression and 4-aminopyridine treatment response

Carlo Wilke(German Center for Neurodegenerative Diseases), Matthis Synofzik(German Center for Neurodegenerative Diseases), Bernard Brais(Montreal Neurological Institute and Hospital), Francesco Saccà(Federico II University Hospital), Matt C. Danzi(University of Miami), Holger Lerche(University of Tübingen), Richard Roxburgh, Orlando Graziani Póvoas Barsottini(Hospital São Paulo), David Pellerin(Montreal Neurological Institute and Hospital), David Mengel(German Center for Neurodegenerative Diseases), Benjamin Bender(University of Tübingen), Jennifer Faber, José Luiz Pedroso(Associação Paulista de Medicina), Filippo M. Santorelli(Fondazione Stella Maris), Andreas Traschütz(German Center for Neurodegenerative Diseases), Lüdger Schöls(German Center for Neurodegenerative Diseases), Henry Houlden(Queen Mary University of London), Paula Camila Alvez, Manuela Neumann(University Children's Hospital Tübingen), Marie‐Josée Dicaire(Institute of Human Genetics), Alessandro Filla(University of Naples Federico II), Ivana Ricca(University of Miami), Stephan Züchner(University of Miami), Chiara Pane(Federico II University Hospital)
Brain
May 11, 2023
Cited by 114


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