Gene augmentation of LCA5-associated Leber congenital amaurosis ameliorates bulge region defects of the photoreceptor ciliary axoneme
Siebren Faber(Radboud University Nijmegen), Ronald Roepman(Radboud University Nijmegen), Marius Ueffing(German Center for Neurodegenerative Diseases), Virginie Hamel(University of Geneva), Katrin Junger(University of Tübingen), Alejandro Garanto(Radboud University Nijmegen), Paul Guichard(University of Geneva), Helen May‐Simera(Johannes Gutenberg University Mainz), Rob W.J. Collin(Radboud University Nijmegen), Karsten Boldt(University Children's Hospital Tübingen), Olivier Mercey(University of Geneva)
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