Healthcare Service Use Patterns Among Patients with Acid Sphingomyelinase Deficiency Type B: A Retrospective US Claims Analysis

Ruth Pulikottil-Jacob(University of Warwick), Natalia Petruski‐Ivleva(AVEO Oncology (United States)), Marie Fournier(Sanofi (France)), Michael L. Ganz(Ithaka Harbors)
Advances in Therapy
March 10, 2023
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