Safety and efficacy of vanzacaftor–tezacaftor–deutivacaftor in adults with cystic fibrosis: randomised, double-blind, controlled, phase 2 trials

Ahmet Uluer(Brigham and Women's Hospital), Gordon MacGregor(Queen Elizabeth University Hospital), Pilar Azevedo(Hospital de Santa Maria), V. Indihar(University of Cincinnati), Claire Keating(Columbia University Irving Medical Center), Marcus Mall(Brigham and Women's Hospital), Edward F. McKone(St. Vincent's University Hospital), Bonnie W. Ramsey(Seattle Children's Hospital), Steven M. Rowe(University of Alabama at Birmingham), Ronald C. Rubenstein(Washington University in St. Louis), Jennifer L. Taylor‐Cousar(National Jewish Health), Elizabeth Tullis(University of Toronto), Lael M. Yonker(Harvard University), Chenghao Chu(Brigham and Women's Hospital), Anna P. Lam(Vertex Pharmaceuticals (United States)), Nitin Nair(Vertex Pharmaceuticals (United States)), Patrick R. Sosnay(Vertex Pharmaceuticals (United States)), Simon Tian(Vertex Pharmaceuticals (United States)), Fredrick Van Goor(Vertex Pharmaceuticals (United States)), Lakshmi Viswanathan(Vertex Pharmaceuticals (United States)), David Waltz(Vertex Pharmaceuticals (United States)), Linda T. Wang(Vertex Pharmaceuticals (United States)), Yingmei Xi(Vertex Pharmaceuticals (United States)), Joanne Billings(University of Minnesota), Alex Horsley(University of Manchester), Alex Horsley(University of Manchester), E.F. Nash, Marleen Bakker, Renske van der Meer, Petrus Merkus, Christof J. Majoor, Karen McCoy, Joanne Billings(University of Minnesota), Krishna Pancham, James Tolle, Bryon Quick, Ahmet Uluer(Brigham and Women's Hospital), Emily DiMango, Adupa Rao, Santiago Reyes, Ross C. Klingsberg, Celeste Barreto, Victor E. Ortega, Donna Beth Willey‐Courand, C. Schwarz, Sivagurunathan Sutharsan, Rainald Fischer, Jane C. Davies, J. Duckers, Alex Horsley(University of Manchester), Simon Doe, E.F. Nash, Marleen Bakker, Harry Heijerman, Renske van der Meer, Petrus Merkus, Christof J. Majoor, George M. Solomon, Christian A. Merlo, Jennifer Griffonnet, Joseph M. Pilewski, Jordan Dunitz, Saba Sheikh, Ronald C. Rubenstein(Washington University in St. Louis), Daniel Rosenbluth, Theodore G. Liou, M.V. Indihar, Krishna Pancham, Lael M. Yonker(Harvard University), Samya Z. Nasr, Jennifer Griffonnet, Cynthia D. Brown, Gregory S. Sawicki, Jennifer Ruddy, Emily DiMango, Bryan Garcia, Andrew T. Braun, Alex H. Gifford, Nighat Mehdi, Maria Tupayachi Ortiz, Raksha Jain, Francisco J. Calimano, Jimmy Johannes, Cori Daines, Jason Fullmer, Joel Mermis, Christopher Barrios, Ngoc P. Ly, Brian Casserly, Stephan Eisenmann, Helge Hebestreit, Alexander Kiefer, Sivagurunathan Sutharsan, Rainald Fischer, Gordon MacGregor(Queen Elizabeth University Hospital), D. Peckham, M.J. Ledson, Eva Van Braeckel, Petrus Merkus, Noel G. McElvaney, Edward F. McKone(St. Vincent's University Hospital), Barry J. Plant, Lucy Burr, Daniel J. Smith, Peter G. Middleton, John Wilson
The Lancet Respiratory Medicine
February 23, 2023
Cited by 63Open Access
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