Efficient in vivo genome editing prevents hypertrophic cardiomyopathy in mice

Daniel Reichart(Brigham and Women's Hospital), Christine E. Seidman(Harvard University), Luk H. Vandenberghe(Massachusetts Eye and Ear Infirmary), Jonathan G. Seidman(Harvard University), Sajeev Kohli(Broad Institute), Gregory A. Newby(Broad Institute), Hiroko Wakimoto(Brigham and Women's Hospital), Lukáš Chmátal(Whitehead Institute for Biomedical Research), David R. Liu(Broad Institute), Júlia Daher Carneiro Marsiglia(ID Genomics (United States)), David C. Page(Howard Hughes Medical Institute), Nerea Zabaleta(Massachusetts Eye and Ear Infirmary), David A. Conner(Howard Hughes Medical Institute), Justin J. Curran(Harvard University), Daniel M. DeLaughter(Howard Hughes Medical Institute), Joshua Gorham(Harvard University), Mingyue Lun(Brigham and Women's Hospital), Aditya Raguram(Broad Institute)
Nature Medicine
February 1, 2023
Cited by 184


Related Papers