Outcome of haematopoietic cell transplantation in children with lysosomal acid lipase deficiency: a study on behalf of the EBMT Inborn Errors Working Party

Su Han Lum(Royal Manchester Children's Hospital), Robert Wynn(Royal Manchester Children's Hospital), Jerry Stein(Schneider Children's Medical Center), Polina Stepensky(Hebrew University of Jerusalem), Ansgar Schulz(University Hospital Ulm), Bernd Gruhn(Jena University Hospital), Cécile Pochon(Université de Lorraine), Michael H. Albert(LMU Klinikum), Karin Mellgren(Sahlgrenska University Hospital), Jane E.R. Potter(Royal Manchester Children's Hospital), Susana Riesco(Instituto de Investigación Biomédica de Salamanca), Sheree Hazelaar(European Society for Blood and Marrow Transplantation), Caroline A. Lindemans(University Medical Center Utrecht), Zühre Kaya(Faculty (United Kingdom)), Simon Jones(Manchester University NHS Foundation Trust), Cristina Díaz de Heredia(Universitat Autònoma de Barcelona), Tiarlan Sirait(European Society for Blood and Marrow Transplantation), Arjan C. Lankester(Leiden University Medical Center), Milen Minkov(Sigmund Freud Privatuniversität Wien), Frédéric Garban(Hôpital Albert Michallon), Miguel Ángel Díaz(Hospital Infantil Universitario Niño Jesús), Bénédicte Neven(Université Paris-Panthéon-Assas), Gérard Michel(Hôpital d'Enfants), Herbert Pichler(St Anna Children's Hospital)
Bone Marrow Transplantation
February 14, 2023
Cited by 9


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