Novel insights into the phenotype and long-term D-gal treatment in PGM1-CDG: a case series
Silvia Radenkovic(VIB-KU Leuven Center for Cancer Biology), Éva Morava(Mayo Clinic), Christin Johnsen(University of Washington), Kaitlin Schwartz(Mayo Clinic in Florida), Gurnoor Lail(University of Toronto), Laura Guilder(University of Toronto), Matthew Schultz(Mayo Clinic in Arizona), Andreas Schulze(University of Toronto), Saadet Mercimek‐Andrews(University of Toronto), Suzanne Boyer(Mayo Clinic in Florida)
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