Taliglucerase-alfa experience with 34 Gaucher disease patients from Turkey
Neslihan Önenli Mungan(Cukurova University), Sema Kalkan Uçar(Ege University), Melike Ersoy(Bakırköy Dr.Sadi Konuk Eğitim ve Araştırma Hastanesi), Mehmet Gündüz(Ministry of Health), Ayşe Çiğdem Aktuğlu Zeybek(Istanbul University-Cerrahpaşa), Deniz Kör(Cukurova University), S. Keskin, Ebru Canda(Ege University), Tuba Eminoğlu, Özlem Ünal Uzun, Mustafa Kılıç, Gonca Kılıç Yıldırım(Eskişehir Osmangazi University), Seda Gunes, Mahmut Çöker(Ege University), Leyla Tümer, Nur Arslan(Dokuz Eylül University)
Cited by 0
Related Papers
A Phase 3 Trial of Sebelipase Alfa in Lysosomal Acid Lipase Deficiency
|New England Journal of Medicine|2015|244
An evaluation of quality of life of mothers of children with enuresis nocturna
|Pediatric Nephrology|2007|71
Efficacy and safety of empagliflozin in glycogen storage disease type Ib: Data from an international questionnaire
|Genetics in Medicine|2022|64