LSD1/PRMT6-targeting gene therapy to attenuate androgen receptor toxic gain-of-function ameliorates spinobulbar muscular atrophy phenotypes in flies and mice

Ramachandran Prakasam(University of Trento), Maria Pennuto(University of Padua)

Nature Communications

February 6, 2023

10.1038/s41467-023-36186-9

Cited by 25

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