<i>N</i>-Substituted <scp>l</scp>-Iminosugars for the Treatment of Sanfilippo Type B SyndromeValeria De Pasquale(University of Naples Federico II), Luigi Michele Pavone(Federico II University Hospital)Journal of Medicinal ChemistryJanuary 25, 202310.1021/acs.jmedchem.2c01617Cited by 14SaveCiteExport RISWatch citationsRelated PapersEGFR activation triggers cellular hypertrophy and lysosomal disease in NAGLU-depleted cardiomyoblasts, mimicking the hallmarks of mucopolysaccharidosis IIIB|Cell Death and Disease|2018|28Metabolic rewiring and autophagy inhibition correct lysosomal storage disease in mucopolysaccharidosis IIIB|iScience|2024|14