Probing the sub-cellular mechanisms of LCA5-Leber Congenital Amaurosis and associated gene therapy with expansion microscopy

Siebren Faber(Radboud University Nijmegen), Ronald Roepman(Radboud University Nijmegen), Marius Ueffing(German Center for Neurodegenerative Diseases), Virginie Hamel(University of Geneva), Katrin Junger(University of Tübingen), Alejandro Garanto(Radboud University Nijmegen), Paul Guichard(University of Geneva), Rob W.J. Collin(Radboud University Nijmegen), Karsten Boldt(University Children's Hospital Tübingen), Olivier Mercey(University of Geneva)
bioRxiv (Cold Spring Harbor Laboratory)
January 18, 2023
Cited by 0


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