Glb1 knockout mouse model shares natural history with type II GM1 gangliosidosis patients

Elena‐Raluca Nicoli(National Institutes of Health), Cynthia J. Tifft(Children's National), Michal Tyrlík(National Institutes of Health), Mohammed Salman Shazeeb(University of Massachusetts Chan Medical School), David A. Priestman(University of Oxford), Yvonne L. Latour(National Institute of Neurological Disorders and Stroke), Jeeva Munasinghe(National Institutes of Health), Anna Luisa Kühn(University of Massachusetts Chan Medical School), Sangwoo T. Han(Johns Hopkins University), Richard L. Proia(National Institute of Diabetes and Digestive and Kidney Diseases), Karolyn Garcia(National Institutes of Health), Robin Yoon(National Institutes of Health), Rohini Sidhu(Washington University in St. Louis), Mylene Huebecker(University of Oxford), Danielle Springer, Eva H. Baker, Josephine Kolstad(University of Massachusetts Chan Medical School), Frances M. Platt(University of Oxford), Morteza Peiravi(National Institutes of Health), Pamela Kell(Washington University in St. Louis), Xuntian Jiang(Washington University in St. Louis), Maria T. Acosta, Martin J. Lizak(National Institutes of Health), Brianna Glase(National Institutes of Health)
Molecular Genetics and Metabolism
January 13, 2023
Cited by 7


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