A breakthrough effect of gene replacement therapy on respiratory outcomes in children with spinal muscular atrophy
Amal Al-Naimi(Qatar Airways (Qatar)), Mutasim Abu‐Hasan(Qatar Airways (Qatar)), Sara G. Hamad(Hamad Medical Corporation), Mahmoud F. El‐Said Osman(Qatar Airways (Qatar)), Reem Mohamed(Hamad Medical Corporation), Khalid Ibrahim, Tawfeg Ben‐Omran(Qatar Airways (Qatar))
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