AAV5-miHTT-mediated huntingtin lowering improves brain health in a Huntington’s disease mouse model
Sarah B. Thomson(University of British Columbia), Blair R. Leavitt(BC Children's Hospital), Alex L. MacKay(University of British Columbia), Da Ma(Shanghai Jiao Tong University), Anouk Stam(UniQure (Netherlands)), Terri L. Petkau(University of British Columbia), Cynthia Brouwers(UniQure (Netherlands)), Astrid Vallès(UniQure (Netherlands)), Sara Mostafavi(Canadian Institute for Advanced Research), Andrew Yung(University of British Columbia Hospital), Melvin M. Evers(UniQure (Netherlands)), Alberto Bresciani(University of Bergamo), Valentina Fodale(IRBM Science Park), Austin M. Hill(University of British Columbia), Piotr Kozłowski(University of British Columbia Hospital), Mirza Faisal Beg(Simon Fraser University), Michael Vermeulen(University of British Columbia), Bretta Russell‐Schulz(University of British Columbia Hospital)
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