CRISPR-mediated correction of skeletal muscle Ca2+ handling in a novel DMD patient-derived pluripotent stem cell model
Cristina Morera(Queen Mary University of London), Yung‐Yao Lin(Queen Mary University of London), Pentao Liu(Hong Kong Science and Technology Parks Corporation), Amaia Paredes‐Redondo(Queen Mary University of London), Denis Rybin(Boston University), Anna Kowala(Queen Mary University of London), Jennifer E. Morgan(Great Ormond Street Hospital), Jinhong Meng(Great Ormond Street Hospital), Jane Owens(Pfizer (United States)), Jihee Kim(Queen Mary University of London), Seth Garren(Pfizer (United States)), Robert Moccia(Pfizer (United States)), Andrew Tinker(Queen Mary University of London), Nicolas Christoforou(Duke University), Francesco Muntoni(Great Ormond Street Hospital), Muriel Nobles(Queen Mary University of London)
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