Onasemnogene Abeparvovec in Type 1 Spinal Muscular Atrophy: A Systematic Review and Meta-Analysis

Carlos Pascual‐Morena(University of Castilla-La Mancha), Vicente Martínez‐Vizcaíno(Universidad Autónoma de Chile), Irene Martínez‐García(University of Castilla-La Mancha), Eva Rodríguez‐Gutiérrez(Servicio de Salud de Castilla La Mancha), Iván Cavero‐Redondo(University of Castilla-La Mancha), Maribel Lucerón‐Lucas‐Torres(University of Castilla-La Mancha)
Human Gene Therapy
September 22, 2022
Cited by 22


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