CRISPR–Cas9-mediated gene editing of the BCL11A enhancer for pediatric β0/β0 transfusion-dependent β-thalassemia

Bin Fu(Central South University), Jiaoyang Liao(East China Normal University), Shuanghong Chen(East China Normal University), Wei Li, Qiudao Wang(East China Normal University), Jian Hu(Central South University), Fei Yang(East China Normal University), Shenlin Hsiao(East China Normal University), Yanhong Jiang(East China Normal University), Liren Wang(East China Normal University), Fangping Chen(Central South University), Yuanjin Zhang(East China Normal University), Xin Wang(East China Normal University), Dali Li(BioScience Laboratories (United States)), Mingyao Liu(BioScience Laboratories (United States)), Yuxuan Wu(East China Normal University)
Nature Medicine
August 1, 2022
Cited by 171

Abstract


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