Clinical and genetic profile of patients enrolled in the Transthyretin Amyloidosis Outcomes Survey (THAOS): 14-year update

Angela Dispenzieri(Mayo Clinic), Soon-Chai Low(Monash University Malaysia), H. Moelgaard(Karolinska University Hospital), Jocelyn Inamo(Centre Hospitalier Universitaire de Martinique), Sanjiv J. Shah(Northwestern University), Olga Azevedo(British Heart Foundation), Eun‐Seok Jeon, Ronald Witteles(Alnylam Pharmaceuticals (United States)), Claudio Rapezzi(University of Ferrara), Dianna Quan(University of Michigan), Giuseppe Vita(University of Messina), Jonas Wixner(Umeå University), Hans Nienhuis(University Medical Center Groningen), Hartmut Schmidt(Université Paris-Sud), Márcia Waddington‐Cruz(Université Paris-Sud), José González‐Costello(British Heart Foundation), Marco Luigetti(Università Cattolica del Sacro Cuore), Mazen Hanna(Cleveland Clinic), Saša Živković(University of Pittsburgh), Doug Chapman(Pfizer (United States)), Yoshiki Sekijima(Shinshu University), Violaine Planté‐Bordeneuve(Université Paris-Est Créteil), David Slosky(Jisc), Daniel J. Lenihan(Saint Francis Medical Center), Samantha LoRusso(Ohio University), Ivaylo Tarnev(Alexandrovska Hospital), Fábio Barroso(Université Paris-Sud), Michele Emdin(Scuola Superiore Sant'Anna), Mathew S. Maurer(Alnylam Pharmaceuticals (United States)), Daniel Jacoby(Baim Institute for Clinical Research), Isabel Conceição(Université Paris-Sud), Scott L. Hummel(VA Ann Arbor Healthcare System), Arnt V. Kristen(Heidelberg University), Francisco Muñoz Beamud(Hospital Juan Ramón Jiménez), Amir Dori(Sheba Medical Center), Brian Drachman(Penn Presbyterian Medical Center), Martha Grogan(Mayo Clinic in Arizona), Juan González‐Moreno, Olivier Lairez(Hôpital Rangueil), Leslie Amass(Pfizer (United States)), Josep Maria Campistol Plana(Hospital Clínic de Barcelona), Calogero Lino Cirami(Azienda Ospedaliero-Universitaria Careggi), David Adams(Mount Sinai Health System), Taro Yamashita(Kanazawa University), Teresa Coelho(Universidade do Porto), Rayomand Press(Karolinska University Hospital), Srinivas Murali(Allegheny General Hospital), Pablo García Pavía(Alexandrovska Hospital), Maria Alejandra Gonzalez Duarte Briseno(Instituto Nacional de Ciencias Médicas y Nutrición Salvador Zubirán)
Orphanet Journal of Rare Diseases
June 18, 2022
Cited by 91


Related Papers